Iyo Bluebird Bio Nhau: Nhau Dzakanaka kubva kuFDA

Uri kutevera iyo Bluebird Bio nhau? Kana usiri, inguva yekupinda mukuziva uye ubatidze zviziviso zvako kune zvese zvazvino zvigadziriso zvine chekuita nekambani iyi. Nekuti inomisikidzwa kuti isvike kumusoro kutsva chero nguva.

Zvinotarisirwa kuti masheya ekambani iyi anogona kunge achikwira zvakanyanya sezvo komiti yevanopa mazano yeFood and Drug Administration (FDA) yakakurudzira bvunzo mbiri dzeiyi kambani yebiotech yekuedza majini marapirwo.

Saka unogona kunge waona mastock ekambani achikwira nekukwira chete. Kuti uwane ruzivo, iyo ticker 'BLUE' yaungave wakaona pazviratidziro ndeyeiyi kambani. Saka zvisinei nemamiriro emusika wese, vagoveri vekambani iyi vari kuwana zororo rinodiwa zvakanyanya.

Yakakosha Bluebird Bio Nhau

Mufananidzo weBluebird bio nhau

Iyi ikambani yeCambridge, Massachusetts-yakavakirwa biotechnology yakatarisana nekugadzira marapirwo emajini kune akanyanya genetic kusagadzikana uye cancer. Pakutanga, mushonga wayo chete wakatenderwa kubva kuEuropean Union (EU) waive Betigeglogene autotemcel iyo inowanzoenda nezita rekuti (Zynteglo).

Kukuyeuchidzai, uyu ndiwo mushonga wechipiri unodhura pasi rose unodhura $1.8 miriyoni. Nekugona kwakawanda kambani yakaona migove yayo ichikwira asi yanga ichidzikira kusvika zvino. Nemvumo yemishonga miviri, inotarisirwa kudzorera chivimbo chakarasika mune ramangwana rayo kubva kune vanoisa mari.

Mamwe mapaipi anoshanda ekambani iyi anosanganisira LentiGlobin gene therapy yeSickle cell chirwere uye Cerebral Adrenoleukodystrophy. IRI kushanda zvakare kurapa Acute Myeloid leukemia, Merkel-cell carcinoma, MAGEA4 mamota akasimba, uye Diffuse hombe B-cell lymphoma.

Kutanga rwendo rwayo seGenetix Pharmaceuticals muna 1992 a brainchild yeMIT faculty nhengo Irving London naPhilippe Leboulch, ichi biotechnology sangano rakaona migove yaro ichikwira kusvika $178.29 muna 2018 uye mushure meizvozvo, vaive padanho rekudonha.

Asi nenhau idzi, migove yakawedzera nezve 28.7% kusvika 4.80 musi weMuvhuro 14 June 2022. Zvitoro zviri munzira yekuwedzera kukuru kwemazana mumakore masere apfuura, maererano nemashoko kubva kuDow Jones Market Data. Zvakakosha kuziva kuti zvikamu zvakaderera pamusoro pe46% gore rino.

Kusvetuka kwehukoshi kunotarisirwa kubva kurudziro yemishonga yemagene ebiotech neFood and Drug Administration. Musi waChikumi 9th Cellular, Tissue, and Gene Therapies Advisory Committee yeFDA yakakurudzira elivadogene autotmcel kana Eli-CEL gene therapy.

Mushonga uyu unoshanda pakurapwa kwechirwere chakabatana neX chromosome, the early active cerebral adrenoleukodystrophy. NeChishanu, sangano rimwe chete rehurumende rakakurudzira Betibeglogene autotemcel kana beti-cel, iyi inguva imwe chete yekurapa yakagadzirirwa kurapa beta-thalassemia varwere.

Mushure mokurapa, hapazovi nekudiwa kwekuwedzerwa kweropa reropa kune varwere vane chirwere chechirwere, avo vanozoda nguva dzose. Iyo FDA inotarisirwa kuita danho repamutemo rebeti-cel musi wa19 Nyamavhuvhu uye zuva reEli-CEL ndi16 Gunyana gore rino.

mhedziso

Nemashoko aya makuru, vanhu vatanga kufarira zvikamu zvekambani uye ichi ndicho chikonzero Bluebird Bio nhau dziri kuita kutenderera munzvimbo dzemari mumisika yose. Hazvina mhosva kuti mutengo unoenda kupi, bluebird inotarisirwa kubatsirwa zvakanyanya kubva kune idzi mazano.

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